Therapeutic homology-independent targeted integration in retina and liver
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DOI: 10.1038/s41467-022-29550-8
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- Koji M. Nishiguchi & Kosuke Fujita & Fuyuki Miya & Shota Katayama & Toru Nakazawa, 2020. "Single AAV-mediated mutation replacement genome editing in limited number of photoreceptors restores vision in mice," Nature Communications, Nature, vol. 11(1), pages 1-9, December.
- Keiichiro Suzuki & Yuji Tsunekawa & Reyna Hernandez-Benitez & Jun Wu & Jie Zhu & Euiseok J. Kim & Fumiyuki Hatanaka & Mako Yamamoto & Toshikazu Araoka & Zhe Li & Masakazu Kurita & Tomoaki Hishida & Mo, 2016. "In vivo genome editing via CRISPR/Cas9 mediated homology-independent targeted integration," Nature, Nature, vol. 540(7631), pages 144-149, December.
- Daniel H. Lackner & Alexia Carré & Paloma M. Guzzardo & Carina Banning & Ramu Mangena & Tom Henley & Sarah Oberndorfer & Bianca V. Gapp & Sebastian M.B. Nijman & Thijn R. Brummelkamp & Tilmann Bürckst, 2015. "A generic strategy for CRISPR-Cas9-mediated gene tagging," Nature Communications, Nature, vol. 6(1), pages 1-7, December.
- A. Barzel & N. K. Paulk & Y. Shi & Y. Huang & K. Chu & F. Zhang & P. N. Valdmanis & L. P. Spector & M. H. Porteus & K. M. Gaensler & M. A. Kay, 2015. "Promoterless gene targeting without nucleases ameliorates haemophilia B in mice," Nature, Nature, vol. 517(7534), pages 360-364, January.
- Andrew V. Anzalone & Peyton B. Randolph & Jessie R. Davis & Alexander A. Sousa & Luke W. Koblan & Jonathan M. Levy & Peter J. Chen & Christopher Wilson & Gregory A. Newby & Aditya Raguram & David R. L, 2019. "Search-and-replace genome editing without double-strand breaks or donor DNA," Nature, Nature, vol. 576(7785), pages 149-157, December.
- Alexis C. Komor & Yongjoo B. Kim & Michael S. Packer & John A. Zuris & David R. Liu, 2016. "Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage," Nature, Nature, vol. 533(7603), pages 420-424, May.
- Hojun Li & Virginia Haurigot & Yannick Doyon & Tianjian Li & Sunnie Y. Wong & Anand S. Bhagwat & Nirav Malani & Xavier M. Anguela & Rajiv Sharma & Lacramiora Ivanciu & Samuel L. Murphy & Jonathan D. F, 2011. "In vivo genome editing restores haemostasis in a mouse model of haemophilia," Nature, Nature, vol. 475(7355), pages 217-221, July.
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