Base-editing corrects metabolic abnormalities in a humanized mouse model for glycogen storage disease type-Ia
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DOI: 10.1038/s41467-024-54108-1
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- Alexis C. Komor & Yongjoo B. Kim & Michael S. Packer & John A. Zuris & David R. Liu, 2016. "Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage," Nature, Nature, vol. 533(7603), pages 420-424, May.
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