IDEAS home Printed from https://ideas.repec.org/p/hpa/wpaper/201001.html
   My bibliography  Save this paper

A Discrete Choice Experiment Investigating Preferences for Funding Drugs Used to Treat Orphan Diseases

Author

Listed:
  • Emmanouil Mentzakis

    (Department of Economics, Centre for Health Economics and Policy Analysis, McMaster University)

  • Patricia Stefanowska

    (Research undertaken while MSc Student, Health Research Methodology and Centre for Health Economics and Policy Analysis, McMaster University)

  • Jeremiah Hurley

    (Department of Economics, Centre for Health Economics and Policy Analysis, McMaster University, Department of Clinical Epidemiology and Biostatistics, McMaster University)

Abstract

Policy debate about funding criteria for drugs used to treat rare, orphan diseases is gaining prominence. This study presents evidence from a discrete choice experiment investigating the preferences of the public regarding public funding for drugs used to treat rare diseases and common diseases using a convenient sample of university students. We find that: other things equal, the respondents do not prefer to have the government spend more for drugs used to treat rare diseases; that respondents are not willing to pay more per life year gained for a rare disease than a common disease; and that the public weighs relevant attributes of the coverage decisions (e.g., costs, disease severity, treatment effectiveness) similarly for both rare and common diseases. The results confirm the importance of severity and treatment effectiveness in preferences for public funding. Though the first study of its kind, the results send a cautionary message regarding the special treatment of orphan drugs in coverage decision making.

Suggested Citation

  • Emmanouil Mentzakis & Patricia Stefanowska & Jeremiah Hurley, 2010. "A Discrete Choice Experiment Investigating Preferences for Funding Drugs Used to Treat Orphan Diseases," Centre for Health Economics and Policy Analysis Working Paper Series 2010-01, Centre for Health Economics and Policy Analysis (CHEPA), McMaster University, Hamilton, Canada.
    • Handle: RePEc:hpa:wpaper:201001
    as

    Download full text from publisher

    File URL: http://chepa.org/docs/working-papers/10-01.pdf
    File Function: First version, 2010
    Download Restriction: no
    ---><---

    References listed on IDEAS

    as
    1. Hole, Arne Risa, 2008. "Modelling heterogeneity in patients' preferences for the attributes of a general practitioner appointment," Journal of Health Economics, Elsevier, vol. 27(4), pages 1078-1094, July.
    Full references (including those not matched with items on IDEAS)

    Citations

    Citations are extracted by the CitEc Project, subscribe to its RSS feed for this item.
    as


    Cited by:

    1. Mortimer, Duncan & Peacock, Stuart, 2012. "Social welfare and the Affordable Care Act: Is it ever optimal to set aside comparative cost?," Social Science & Medicine, Elsevier, vol. 75(7), pages 1156-1162.

    Most related items

    These are the items that most often cite the same works as this one and are cited by the same works as this one.
    1. Yamada, Katsunori & Sato, Masayuki, 2013. "Another avenue for anatomy of income comparisons: Evidence from hypothetical choice experiments," Journal of Economic Behavior & Organization, Elsevier, vol. 89(C), pages 35-57.
    2. Joachim Marti, 2012. "Assessing preferences for improved smoking cessation medications: a discrete choice experiment," The European Journal of Health Economics, Springer;Deutsche Gesellschaft für Gesundheitsökonomie (DGGÖ), vol. 13(5), pages 533-548, October.
    3. Epstein, Andrew J., 2010. "Effects of report cards on referral patterns to cardiac surgeons," Journal of Health Economics, Elsevier, vol. 29(5), pages 718-731, September.
    4. Hsin‐Fan Chen & Sheng‐Hung Chen & Jie‐Min Lee & Huei‐Yann Jeng, 2010. "Who Are the Potential Smokers of Smuggled Cigarettes?," Asian Economic Journal, East Asian Economic Association, vol. 24(3), pages 221-234, September.
    5. Jennifer A Whitty & Simon Stewart & Melinda J Carrington & Alicia Calderone & Thomas Marwick & John D Horowitz & Henry Krum & Patricia M Davidson & Peter S Macdonald & Christopher Reid & Paul A Scuffh, 2013. "Patient Preferences and Willingness-To-Pay for a Home or Clinic Based Program of Chronic Heart Failure Management: Findings from the Which? Trial," PLOS ONE, Public Library of Science, vol. 8(3), pages 1-8, March.
    6. Arne Hole & Julie Kolstad, 2012. "Mixed logit estimation of willingness to pay distributions: a comparison of models in preference and WTP space using data from a health-related choice experiment," Empirical Economics, Springer, vol. 42(2), pages 445-469, April.
    7. Determann, Domino & Lambooij, Mattijs S. & de Bekker-Grob, Esther W. & Hayen, Arthur P. & Varkevisser, Marco & Schut, Frederik T. & Wit, G. Ardine de, 2016. "What health plans do people prefer? The trade-off between premium and provider choice," Social Science & Medicine, Elsevier, vol. 165(C), pages 10-18.
    8. Peter Sivey, 2012. "The effect of waiting time and distance on hospital choice for English cataract patients," Health Economics, John Wiley & Sons, Ltd., vol. 21(4), pages 444-456, April.
    9. Martine Audibert & Yong He & Jacky Mathonnat, 2013. "Two-Period Comparison of Healthcare Demand with Income Growth and Population Aging in Rural China: Implications for Adjustment of the Healthcare Supply and Development," Working Papers halshs-00846088, HAL.
    10. Chung, Sol & Agnew, Julie & Bateman, Hazel & Eckert, Christine & Liu, Junhao & Thorp, Susan, 2024. "The impact of mortgage broker use on borrower confusion and preferences," Journal of Economic Behavior & Organization, Elsevier, vol. 224(C), pages 229-247.
    11. Emmanouil Mentzakis & Mandy Ryan & Paul McNamee, 2011. "Using discrete choice experiments to value informal care tasks: exploring preference heterogeneity," Health Economics, John Wiley & Sons, Ltd., vol. 20(8), pages 930-944, August.
    12. Carole Ropars-Collet & Mélody Leplat & Philippe Le Goffe & Marie Lesueur, 2015. "La pêche professionnelle est-elle un facteur d’attractivité récréative sur le littoral ?," Revue économique, Presses de Sciences-Po, vol. 66(4), pages 729-754.
    13. Schaafsma, Marije & Brouwer, Roy & Liekens, Inge & De Nocker, Leo, 2014. "Temporal stability of preferences and willingness to pay for natural areas in choice experiments: A test–retest," Resource and Energy Economics, Elsevier, vol. 38(C), pages 243-260.
    14. Landmann, D. & Feil, J.-H. & Lagerkvist, C.J. & Otter, V., 2018. "Designing capacity development activities of small-scale farmers in developing countries based on discrete choice experiments," 2018 Conference, July 28-August 2, 2018, Vancouver, British Columbia 277738, International Association of Agricultural Economists.
    15. Kløjgaard, Mirja Elisabeth & Hess, Stephane, 2014. "Understanding the formation and influence of attitudes in patients' treatment choices for lower back pain: Testing the benefits of a hybrid choice model approach," Social Science & Medicine, Elsevier, vol. 114(C), pages 138-150.
    16. Gillespie Rob & Kragt Marit E., 2012. "Accounting for Nonmarket Impacts in a Benefit-Cost Analysis of Underground Coal Mining in New South Wales, Australia," Journal of Benefit-Cost Analysis, De Gruyter, vol. 3(2), pages 1-29, May.
    17. Martine AUDIBERT & Yong HE & Jacky MATHONNAT, 2017. "What does demand heterogeneity tell us about health care provider choice in rural China?," Working Papers P193, FERDI.
    18. Pedro Ramos & Hélio Alves & Paulo Guimarães & Maria A. Ferreira, 2017. "Junior doctors’ medical specialty and practice location choice: simulating policies to overcome regional inequalities," The European Journal of Health Economics, Springer;Deutsche Gesellschaft für Gesundheitsökonomie (DGGÖ), vol. 18(8), pages 1013-1030, November.
    19. Rahman, Md. Hasanur & Majumder, Shapan Chandra & Debbarman, Shantanu, 2020. "Examine the Role of Agriculture to Mitigate the CO2 Emission in Bangladesh," Asian Journal of Agriculture and Rural Development, Asian Economic and Social Society (AESS), vol. 10(01), January.
    20. Hynes, Stephen & Tinch, Dugald & Hanley, Nick, 2013. "Estimating the value of improvements to coastal waters resulting from revisions of the EU Bathing Waters Directive," Working Papers 160058, National University of Ireland, Galway, Socio-Economic Marine Research Unit.

    More about this item

    Statistics

    Access and download statistics

    Corrections

    All material on this site has been provided by the respective publishers and authors. You can help correct errors and omissions. When requesting a correction, please mention this item's handle: RePEc:hpa:wpaper:201001. See general information about how to correct material in RePEc.

    If you have authored this item and are not yet registered with RePEc, we encourage you to do it here. This allows to link your profile to this item. It also allows you to accept potential citations to this item that we are uncertain about.

    If CitEc recognized a bibliographic reference but did not link an item in RePEc to it, you can help with this form .

    If you know of missing items citing this one, you can help us creating those links by adding the relevant references in the same way as above, for each refering item. If you are a registered author of this item, you may also want to check the "citations" tab in your RePEc Author Service profile, as there may be some citations waiting for confirmation.

    For technical questions regarding this item, or to correct its authors, title, abstract, bibliographic or download information, contact: Lyn Sauberli (email available below). General contact details of provider: https://edirc.repec.org/data/chepaca.html .

    Please note that corrections may take a couple of weeks to filter through the various RePEc services.

    IDEAS is a RePEc service. RePEc uses bibliographic data supplied by the respective publishers.